Panel Discussion: Clinical Development Processes for Rare Disorders: Moving Towards a Patient-Driven Approach
Time: 1:30 pm
day: Day One
Details:
- The unique challenges faced in attaining treatments by patients with rare disorders
- Where patient perspectives can be conducive to success in the clinical trial endpoint design of therapies for rare disorders
- Good and bad clinical development stories from trials taking different approaches to patient advocacy input
- The case behind biotech and pharma incorporating patient perspective early in their drug development processes
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