Christina Ohnsman

Company: REGENXBIO
Job title: Senior Clinical Development Lead
Seminars:
Choosing a Suitable Comparator in a Rare Disease Trial 1:30 pm
Regulators require comparators but often placebo controls in rare disease trials are not ethical or practical Exploring the role natural history studies can play Understanding regulatory requirements of suitable comparatorsRead more
day: Day Two
Panel Discussion: Defining Clinical Endpoints for Rare Diseases 2:00 pm
Incorporating patient perspectives to define a suitable primary endpoint Assessing measurability as a factor in endpoint choice Navigating challenges of clinical trial design with a small patient populationRead more
day: Day Two