Speaker Faculty

Inês Alves

Patient Expert & Member of the Committee for Orphan Medicinal Products

EMA

Eva Andres-Mateos

Senior Director of Translational Research

Atsena Therapeutics

Stuart Beattie

Gene Therapy Global Regulatory CMC

Biogen

P.J. Brooks

Acting Director, Office of Rare Diseases Research, NCATS

NIH

Angelo Loris

Brunetta Coordinator Italian Associations

Advocacy Council

Gloria Palomo Carrasco

Non-Clinical Assessor, AEMPS; Member of the Committee for Orphan Medicinal Products, EMA

AEMPS, EMA

David Dobnik

Senior Research Associate, NIB & Chief Scientific Officer, Niba Labs

Slovenian National Institute of Biology

Anne Douar

Chief Development Officer

Vivet Therapeutics

Niklas Engler

Head Cell and Gene Therapy Strategy

Roche

Thijs Gerritzen

Principal Scientist Process Development

Amarna Therapeutics B.V.

Ivan Gorbachov

Senior Director

Novartis

Markus Haindl

Global Head Of Gene Therapy & Technical Development

Roche

Harm Hermsen

Vice President, Global Regulatory Affairs

UniQure

John Johnston

Clinical Assessor, Biologicals Unit

MHRA

Niamh Kinsella

Global Regulatory CMC Early Development Gene Therapy Lead

Biogen

Nathalie Lambot

Public Health Advisor: Clinical Trials – Regulatory Affairs

pharma.be

Amanda Rivière

Manager Regulatory Affairs

Genethon

Valérie Salentey

Director of Regulatory Affairs & Quality Assurance

Sensorion

Oscar Segurado

Chief Medical Officer

ASC Therapeutics

Violeta Stoyanova- Beninska

Chair of Committee for Orphan Medicinal Products

EMA

Magali Taiel

Chief Medical Officer

GenSight Biologics

Speaker To Be Confirmed

The Jackson Laboratory

Speaker To Be Confirmed

Thread Research

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